There are three other main types of NCL, including two forms that begin earlier in childhood and a very rare form that strikes adults. The symptoms of these three types are similar to those caused by ...

Chauncey grew up on a farm in rural northern California. At 18 he ran away and saw the world with a backpack and a credit card, discovering that the true value of any point or mile is the experience ...

Amicus Therapeutics is moving on from an early-phase Batten disease program after follow-up data showed the therapy didn't stop the fatal nervous system disease from progressing long-term. The company ...

The U.S. Food and Drug Administration has approved Brineura (cerliponase alfa) to treat a specific form of Batten Disease, a condition that typically starts between 2 and 4 years of age. The newly ...

LINCOLN, Neb. (KOLN) — This weekend, hundreds of people gathered in Lincoln for a conference dealing with Batten Disease. It’s rare, it’s always deadly — and there is still no cure — affecting only a ...